Achondroplasia is a rare genetic disorder that causes short stature and bowed legs. It is the result of a genetic mutation that is more likely to arise in the children of older men. In this article, ...
Emerging biologic therapies and surgical innovations are driving growth in the achondroplasia treatment market. Opportunities ...
Achondroplasia is a genetic condition that affects the body’s ability to convert cartilage into bone, resulting in short limbs. The condition is caused by changes to the FGFR3 gene, which can pass ...
Credit: Getty Images. The approval was based on data from a phase 3 study that evaluated the efficacy and safety of Voxzogo in 121 children with genetically-confirmed achondroplasia. The Food and Drug ...
The oral FGFR1-3 selective tyrosine kinase inhibitor infigratinib was found to be safe and effective at the highest studied dose among children with achondroplasia in a phase II dose-finding study.
Skeletal dysplasia is the broad term for conditions that cause problems with the way bones and cartilage grow. Achondroplasia dwarfism is the most common type of skeletal dysplasia. Achondroplasia ...
Ascendis Pharma's Yorvipath and Skytrofa drove Q3 revenues to €213.6 million, nearly quadrupling year-over-year. Read why ...
Achondroplasia is a type of dwarfism that affects the growth in children, leading to a short stature or small size. Achondroplasia is a rare genetic condition that affects one in every 15,000 to ...
The Food and Drug Administration approved the first treatment for the most common cause of dwarfism Friday, a drug that has proved to increase children’s height but has been polarizing among adults ...
Q: Which doctor can I consult if my baby is diagnosed with achondroplasia? A: You will have to consult a pediatrician, orthopedic surgeon, dental surgeon and a neurosurgeon depending on the ...