Inside every human cell, a tiny structure called a lysosome acts like a recycling center, breaking down toxic waste, clearing ...

JCR presented new clinical data in a poster session at the 18th International Symposium on MPS and Related Lysosomal Diseases, held June 4-7, 2026.

Collaboration will evaluate Scenic's first-in-class PLA2G15 inhibitor program in Parkinson's diseaseLeveraging MJFF’s LITE ...

JCR Pharmaceuticals Co., Ltd. (TSE 4552; “JCR”), a global specialty biopharmaceutical company dedicated to developing therapies for rare and genetic diseases, announced today that it will present new ...

Rare diseases often remain undetected for years, mostly because of limited awareness and complex symptoms that are not easy to diagnose. One such group of conditions is Lysosomal Storage Disorders, or ...

Functioning brain cells need a functioning system for picking up the trash and sorting the recycling. But when lysosomes, the cellular sanitation machines responsible for those tasks, break down or ...

The selected projects demonstrated significant potential to address unmet needs within these rare communities. The recipients include: Fabry disease: Mitra Tavakoli, University of Exeter, Exeter, UK, ...

Looking at lysosomes Dysfunction in the lysosome, an organelle inside cells, has been implicated in neurodegenerative diseases. So the Stanford team has been studying the organelle for clues to ...

Stanford researchers constructed an atlas of the proteins found in the lysosome across different brain cell types, a recently published paper reported. Lysosomes are cell organelles that play ...

LONDON--(BUSINESS WIRE)--Technavio’s latest market research report on the global lysosomal storage diseases (LSDs) market provides an analysis of the most important trends expected to impact the ...