Italian researchers found that 62% of patients with early-stage Huntington disease (HD) lacked insight into their motor ...
The US Food and Drug Administration (FDA) has accepted a supplemental New Drug Application for nebulized treprostinil for the ...
The safety profile has generally been manageable, although cytopenias, gastrointestinal symptoms, and differentiation ...
Progressive pulmonary fibrosis (PPF) is undercoded and underrecognized, according to electronic health record evidence.
In a new study, nearly half of individuals with NF1 had cherry angiomas, suggesting a previously unrecognized link.
A woman living with HAE recalls her worst swelling episode yet and how it has affected the way she views the good days.
Analysis of a national registry of hospital data found racial gaps in blood transfusion rates among patients hospitalized for ...
Comprehensive care is about assessing each patient’s needs and bringing the right professionals to the table. No two cases of ...
Survey responses revealed a notable disconnect between how patients with PNH and their physicians perceive symptoms, ...
Younger patients with MDS had lower-risk disease features and significantly better overall and leukemia-free survival.
A woman with hypoplastic low-risk MDS had reversible cytopenic flares in 2 pregnancies, with blood counts returning to normal ...
According to a RITAZAREM trial analysis, a subgroup of patients with relapsing AAV show a suboptimal response to rituximab ...