A case of SM-AHN involving aCML revealed spontaneous tumor lysis syndrome before cytoreductive therapy was started.
A case report describes the successful treatment of CAS secondary to chronic CLL using combination sutimlimab and ...
Three respiratory questionnaires correlate well with the severity of ILD and IPF at baseline but not with disease progression ...
A mother caring for 2 sons with FSGS affirms the correlation between a patient's support system and their ability to manage ...
Multidisciplinary vigilance is necessary during the treatment of SM in order to differentiate nodal changes from disease ...
In a mouse model of NF1, KRAS inhibition reduced plexiform neurofibroma burden, especially when combined with MEK inhibition.
A case of familial chylomicronemia syndrome (FCS) recently described in the International Journal of Clinical Biochemistry ...
Vor Bio announced the completion of enrollment in the UPSTREAM MG trial of telitacicept and described plans for a new trial ...
Applying the ILAE 2022 criteria may promote earlier recognition of evolving Lennox-Gastaut syndrome (LGS), enabling prompt ...
Many patients with FA suffer from sleep apnea. Will using a CPAP machine help? A patient weighs in on the matter.
A woman living with SM shares what led her to advocacy work and why she believes training in rare diseases is important.
A woman living with GPP explains how this rare disease has changed her skin and the tactics she's using to combat the effects ...
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